StudyFinder
Synergistic Enteral Regimen for Treatment of the Gangliosidoses (SYNER-G)
Recruiting
The Syner-G regimen research study seeks to evaluate the use of a combination of a medication called miglustat and a ketogenic diet for treatment of the gangliosidoses to learn if this combination will provide improved clinical outcomes compared to what we currently know about the natural course of the disease.
Up to 18 years old
Inclusion Criteria:
• no more than 17 years old
• documented infantile or juvenile gangliosidosis disease
Exclusion Criteria:
• severe kidney disease
• females who are pregnant or breast feeding
• females who are post puberty who are unwilling to use highly effective birth control
Rare Diseases
GM1 Gangliosidoses, GM2 Gangliosidoses, Sandhoff Disease, Tay-Sachs Disease
Jeanine Jarnes - utzx0002@umn.edu
Jeanine Jarnes
PHASE4
1311M46101
20890
See this study on ClinicalTrials.gov